Miplyffa (arimoclomol)
Orphan
- Region
- 🇪🇺 EU
- Active substance
- arimoclomol
- Company
- Orphazyme A/S
- Status
- Application withdrawn
- Therapeutic area
- Niemann-Pick Disease, Type C
- Designations
- Orphan
- Application
- EMEA/H/C/005203
- ATC
- N07
- Official record
- www.ema.europa.eu
Indication
Treatment of Niemann-Pick disease type C (NPC).
Regulatory milestones
No milestones recorded in the last year.
Same substance in other markets
- 🇪🇺 Meplyffa Refused · Zevra Denmark A/S
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Information from official EMA, FDA, Federal Register and SEC records. Dates marked company-announced come from the company's own SEC filing; dates marked estimate are calculated, not official. Not investment or medical advice; always confirm on the source.